Joe(@Gantosj) 's Twitter Profile Photo

Good note from Mizuho!
$SRPT receipt of a draft-label is very positive signal fro review
There is likely a united front at the FDA as we had seen in the past 3 months from Dr. Marks!

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PIENSAPRENSA 346,6 mil Seguidores(@PiensaPrensa) 's Twitter Profile Photo

Madre de 'Tomás contra Duchenne' alcanza los 3 mil millones de pesos tras su paso por el Biobío.
El objetivo de la caminata de Gómez, es un tratamiento para Tomás. El niño de 5 años padece distrofia muscular de Duchenne, de la que podría recuperarse al acceder al Elevidys.
El

Madre de 'Tomás contra Duchenne' alcanza los 3 mil millones de pesos tras su paso por el Biobío.
El objetivo de la caminata de Gómez, es un tratamiento para Tomás. El niño de 5 años padece distrofia muscular de Duchenne, de la que podría recuperarse al acceder al Elevidys.
El
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Jennifer Handt(@JenniferHandt) 's Twitter Profile Photo

This really gets to the ❤️ of the issue. This video of my son treated with Elevidys was captured this a.m. Ignore the outrageous PJs-socks combo. Don't tell me his improvement with this treatment matters less than your pencil-pushing narrative. Don't.

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Joe(@Gantosj) 's Twitter Profile Photo

$SRPT Label expansion is a fact, time for the U.S. FDA decision

'We assume an 80% to 90% of label expansion probability for to all ambulatory boys' Oppenheimer analyst Hartaj Singh wrote as he upgraded $SRPT to Outperform from Perform with an $180 per share target

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Odair Cunha(@odaircunhamg) 's Twitter Profile Photo

SALVE O ENRICO!

Ótima notícia para Marina, Eric e Enrico: a ordem bancária para o pagamento de R$ 17.203.200,00 para a compra do Elevidys foi feita! Isso significa que os recursos para o medicamento do Enrico estão garantidos! Parabéns a todos que estão juntos nessa batalha pela

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babi(@tylercismo) 's Twitter Profile Photo

oi gente! na escola onde eu trabalho tem um aluno com distrofia muscular de duchenne, é uma síndrome que não tem cura e surgiu um tratamento que não existe no brasil ainda, quem puder por favor assinar essa petição ajudaria muito 🫶 change.org/p/sarepta-por-…

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Joe(@Gantosj) 's Twitter Profile Photo

$SRPT no news yet... But it is very close!

I doubt to see Dr. Marks attending the large CureDuchenne conference on May 24th & no approval yet!

'We’re also honored to include Dr. Marks as our keynote speaker, allowing families to hear the latest on approvals directly

$SRPT no news yet... But it is very close!

I doubt to see Dr. Marks attending the large CureDuchenne conference on May 24th & no #Elevidys approval yet!

'We’re also honored to include Dr. Marks as our keynote speaker, allowing  families to hear the latest on approvals directly
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quantumup(@Quantumup1) 's Twitter Profile Photo

Citi open a Catalyst Watch for $SRPT (Buy/$172) 'on the potential full approval of Elevidys for the treatment of Duchenne muscular dystrophy (DMD) and expansion of the drug label beyond the current restricted 4-5-year-old population by the PDUFA target date of June 21, 2024:'

Citi open a Catalyst Watch for $SRPT (Buy/$172) 'on the potential full approval of Elevidys for the treatment of Duchenne muscular dystrophy (DMD) and expansion of the drug label beyond the current restricted 4-5-year-old population by the PDUFA target date of June 21, 2024:'
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Jon(@JonU235) 's Twitter Profile Photo

$SRPT On the cover Washington FAMILY magazine: Hiram Secrist, first in the nation to commercially receive for : “This is six months out, and that these are the things that he’s able to do, it’s been incredible.” Children's National Hospital 🏥 FDA Biologics washingtonfamily.com/nova-6-year-ol…

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quantumup(@Quantumup1) 's Twitter Profile Photo

Morgan Stanley Names $SRPT a Catalyst Driven Idea; see an 85% probability of a positive outcome, w/ $SRPT potentially up 27%-50%, on their Base Case Assumption of FDA Label Expansion to Ambulatory Patients of all Ages:

Morgan Stanley Names $SRPT a Catalyst Driven Idea; see an 85% probability of a positive outcome, w/ $SRPT potentially up 27%-50%, on their Base Case #Elevidys Assumption of FDA Label Expansion to Ambulatory Patients of all Ages:
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Ali Albusaidi(@asa_albusaidi) 's Twitter Profile Photo

🔴مساعدة علاجية عاجلة🔴
طفل يبلغ من (5 سنوات)
مصاب بمرض
دوشين (DMD) خلل جين رقم 45
وبحاجة لحقنة دواء ( ELEVIDYS)
بشكل عاجل لتجنب إصابته بضمور وضعف العضلات والشلل
*رابط التبرع:
jood.om/ar/Donate/Camp…
* رابط الحاله ( تويتر ):
x.com/sulaiman_oman5

🔴مساعدة علاجية عاجلة🔴
طفل يبلغ من (5 سنوات)
مصاب بمرض 
دوشين (DMD) خلل جين رقم 45
وبحاجة لحقنة دواء ( ELEVIDYS)
بشكل عاجل لتجنب إصابته بضمور وضعف العضلات والشلل
*رابط التبرع:
jood.om/ar/Donate/Camp…
* رابط الحاله ( تويتر  ):
x.com/sulaiman_oman5
#علاج_سليمان #السيد_الجليلة
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Marisela Santibáñez Novoa(@mariseka) 's Twitter Profile Photo

Doctor Tomás Lagomarsino 🚶🏾‍♀️ diputado Doctor Tomás Lagomarsino en octubre 2023 fracasó en el ensayo en fase avanzanda, planteando dudas a La FDA de EE.UU en su aprobación acelerada y revisará la terapia génica para Duchenne de Sarepta para su aprobación tradicional
(16 de febrero 2024) ALGO tan

@DrLagomarsino 🚶🏾‍♀️#TomasRoss diputado @DrLagomarsino en octubre 2023 #Elevidys fracasó en el ensayo en fase avanzanda, planteando dudas a La FDA de EE.UU en su aprobación acelerada y revisará la terapia génica para Duchenne de Sarepta para su aprobación tradicional
(16 de febrero 2024) ALGO tan
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Jon(@JonU235) 's Twitter Profile Photo

$SRPT ' is available now in America and we have been accepted but it requires us to have proof of funds.' (More importantly: stem cell therapy is a scam! Repeat after me! Scam! Spread the word global Duchenne community!)😢worldduchenne.org/news/warning-o…

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🐎 🇵🇸هۛدوء 𐬛 خـ͓̽ـيـ͓̽ـآلَ(@a16g23) 's Twitter Profile Photo

مصاب بمرض دوشين الحثل العضلي ( الخلل في الجين ٤٥ الغير وراثي ) سعر الحقنة مليون ريال عُماني ( حقنة Elevidys ) وهذا الدواء مصمم بأنه يؤخذ مرة وحدة بالحياة ، لازم سليمان ياخذها قبل تاريخ ٢٥.٦.٢٢٤ وإلا بيصاب بالشلل والضمور العضلي❤️‍🩹

مصاب بمرض دوشين الحثل العضلي ( الخلل في الجين ٤٥ الغير وراثي ) سعر الحقنة مليون ريال عُماني ( حقنة Elevidys ) وهذا الدواء مصمم بأنه يؤخذ مرة وحدة بالحياة ، لازم سليمان ياخذها قبل  تاريخ ٢٥.٦.٢٢٤ وإلا بيصاب بالشلل والضمور العضلي❤️‍🩹
#انقذوا_سليمان
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Tom Silver(@TomSilver39) 's Twitter Profile Photo

JPM:' $SRPT Scenario Table & Upside / Downside Considerations
Related To Elevidys Label Expansion; TP=increased to $177 from $112 prior...'

JPM:' $SRPT Scenario Table & Upside / Downside Considerations
Related To Elevidys Label Expansion; TP=increased to $177 from $112 prior...'
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Jon(@JonU235) 's Twitter Profile Photo

$SRPT Micah Norby: diagnosed with February 9th, insurance denial, appealed, dosed April 16th, one day before turning 6, first commercial dose in Iowa. Creston News Advertiser FDA Biologics University of Iowa Health Care 💪crestonnews.com/adair-county-f…

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@DiestraySiniestra(@SinTraidoras) 's Twitter Profile Photo

SABÍA Vlado Mirosevic q la FDA 🇺🇸 revisará la terapia A.M Duchenne para su aprobación tradicional pues en octubre Elevidys fracasó en el objetivo de un ensayo en fase avanzada, lo que planteó dudas sobre la aprobación tradicional de la terapia en EEUU es.marketscreener.com/cotizacion/acc…

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Jon(@JonU235) 's Twitter Profile Photo

$SRPT The Bafus Family's phenomenal video series goes well beyond the discussion - they share the totality of highs and lows of a family coping with a . Global Genes NORD Muscular Dystrophy Association EveryLife Foundation youtube.com/@BafusFamily/v…

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